2

Spinal Muscular Atrophy: Entering the Treatment Age

Année:
2018
Langue:
english
Fichier:
PDF, 390 KB
english, 2018
7

Challenges ahead for trials in Friedreich’s ataxia

Année:
2016
Langue:
english
Fichier:
PDF, 91 KB
english, 2016
8

Inherited Neuromuscular Disorders: Presentation, Diagnosis, and Advances in Treatment

Année:
2017
Langue:
english
Fichier:
PDF, 362 KB
english, 2017
9

Pediatric Ataxia: Focus on Chronic Disordersca

Année:
2018
Langue:
english
Fichier:
PDF, 800 KB
english, 2018
10

Frataxin Restoration in the Nervous System: Possibilities for Gene Therapy

Année:
2018
Langue:
english
Fichier:
PDF, 140 KB
english, 2018